Spinal Muscular Atrophy (SMA) Type 1 Survival Without New Pharmacotherapies: Two Treatment Paradigms
Description
CONCLUSION: Medical treatments begun during the first 6 weeks of age convert SMA1 into SMA2 or 3 but cough flows remain inadequate to avoid many pneumonias that, once resolved by a treatment paradigm of extubation to CNVS and MIE, eliminates need to
